As the flurry of executive orders continues to flow from the White House, leaving in its wake chaos and confusion across the ...

Once high-flying Bluebird Bio Inc. has found a way out of its financial squeeze, as funds managed by global investment firms ...

In response to the news of reported layoffs at the U.S. FDA over the weekend, Advanced Medical Association president and CEO ...

Researchers from Columbia University Irving Medical Center and collaborators applied unbiased scRNA-seq to study Lepr ...

Gene therapy specialist Meiragtx Holdings plc is heading for its first marketing approval following the successful treatment ...

Roche Holding AG revealed plans to launch its sequencing by expansion technology next year, raising the possibility that ...

Using ALK+ lung cancer patient-derived cell lines, researchers have performed phosphoproteomic screening and identified ...

EG 427 SAS has closed a €27 million (US$28.3 million) series B round, which will fund it to completion of the first clinical ...

A paper published in The Lancet showed that four out of four young children with Leber congenital amaurosis 4 retinal dystrophy due to a genetic deficiency of Aryl-hydrocarbon-interacting protein-like ...

Approxima Srl raised €7.3 million (US$7.65 million) in the first close of its series A financing round for its tricuspid valve repair system which is based on reshaping the right ventricle.

In a recently published study, researchers from Cima Universidad de Navarra and collaborators presented a novel SdAb-based ...

Though it’s been used off-label for more than three decades to treat cerebrotendinous xanthomatosis, Mirum Pharmaceuticals Inc.’s chenodiol gained an official U.S. FDA nod Feb. 21 as the first drug ...