Illinois couple Megan Kempf and Kyle are parents to Poppy, 9, and Oliver, 2, who suffer from a dementia-like condition called ...

A new study reveals a critical vulnerability in a brain receptor targeted by a rare autoimmune disease. Researchers have ...

Discover Tobie Goh's inspiring journey through multiple craniofacial surgeries to overcome Crouzon Syndrome and achieve a ...

While deadly diseases had some pretty terrible outcomes throughout history, they also have led the way for incredible scientific research, discovery, and medical advancement. Join Hank Green for a new ...

A "gene silencer" (technically known as small interfering RNA, or siRNA), locally delivered by nanoparticles embedded in an ...

At the World Economic Forum, CEO Stéphane Bancel expressed concern about the US vaccine market but remained committed to ...

Pam Kowalczyk struggles with the genetic condition PKU, which prevents the body from processing protein. Years ago, she ...

Williams-Beuren syndrome is a rare, congenital disease in which the main morbidity and mortality comes from obstructions, or ...

Eton Pharmaceuticals, Inc. is rated Buy with revenue growth, FCF positivity & declining SG&A margins support. Learn more ...

The FDA’s rare pediatric disease priority review voucher program missed reauthorization at the last minute in 2024; advocates ...

A new study confirms this long-held theory, discovering that 60 percent of defective genetic pairs impacting the production ...

Together with colleagues from Stanford University, USA, researchers at the Leibniz Institute on Aging - Fritz Lipmann Institute (FLI) have, for the first time, created a comprehensive cell ...