Peake relates the story of folk music legend Woody Guthrie, "our greatest advocate," if only by accident. The ...

In a trial of people with early Huntington's, the newly developed therapy slowed the progression of symptoms by 75%. Reading time 3 minutes Doctors in the UK are claiming to have performed a ...

US regulators laid out new guidelines for approving custom-made treatments for individual patients, a move that could bring ...

(CNN) - There may be some hope for those living with Huntington’s disease after a new experimental gene therapy was reportedly found to slow the progression of the disease. Drugmaker Uniqure announced ...

"I am absolutely thrilled and excited that we now have a potential treatment for this truly devastating disorder and what the data means is that for a person who has Huntington's disease, they will be ...

UCL and uniQure report the first treatment to slow Huntington’s disease with gene therapy AMT-130. High-dose patients had 75% less progression over three years compared with standard care. uniQure ...