The agency's decision is based on results from a clinical trial in which the treatment improved hearing in 80 percent of the ...

Danish dermatology specialist Leo Pharma is paying $50 million for U.S. gene writing biotech Replay and its preclinical gene ...

A first-of-its-kind gene therapy that can restore hearing in children born deaf has just cleared its final hurdle—and, in a ...

A gene therapy pioneer whose invention was pivotal to a first-of-its-kind personalized gene-editing treatment for a Philadelphia-area infant is among the winners of this year’s Franklin Institute ...

As early results show promise, the 23-year-old hopes the treatment could finally clear a path toward his dream of becoming ...

An experimental gene therapy for a rare form of genetic deafness has successfully restored hearing in children and adults, ...

Kelly Anne is a deputy editor at Forbes Advisor overseeing the development of various initiatives, including newsletters, ...

Regeneron’s drug restored hearing in 11 of 12 children in a rare, inherited condition that causes deafness.

The treatment, the first of its kind, was approved by the Food and Drug Administration on Thursday. “Our baby was born deaf, ...

Intellia Therapeutics, a leading biotechnology company, announced that its CRISPR-based treatment for a rare swelling ...

The treatment, developed by Regeneron Pharmaceuticals, is for a very rare form of deafness. But it represents a medical ...

Cell and gene therapies are currently niche products, even within specialty pharmacy, drugs that, by most definitions, are ...