Intellia Therapeutics, a leading biotechnology company, announced that its CRISPR-based treatment for a rare swelling ...

The ethics of using safe gene therapies to improve the health and cognition of Down syndrome children and adults.

The biotech's candidate may treat a great number of illnesses that have one thing in common.

A CRISPR Therapy Just Cured A Disease From Inside The Body For The First Time. The Gene-Editing Era Officially Started Monday ...

Intellia Therapeutics said its Crispr-based treatment for hereditary angioedema met its goals in a Phase 3 trial, marking a ...

Scribe Therapeutics to highlight engineered CRISPR platform advances and lead cardiometabolic pipeline at ASGCT and EAS Congress 2026 ...

CRISPR Therapeutics is reporting encouraging early results from trials of its CAR T cell therapy, zugo-cel, in autoimmune diseases such as lupus and systemic sclerosis. The therapy, developed using ...

A phase 3 trial of Intellia Therapeutics’ in vivo gene-editing therapy lonvoguran ziclumeran (lonvo-z) has hit its primary ...

Two papers published in The New England Journal of Medicine highlight the potential of gene editing for treatment of sickle ...

Researchers have used modified CRISPR to silence the extra chromosome 21 in Down syndrome cells, showing promising ...

JMIR Publications today featured two new stories in its News and Perspectives section, highlighting a shift toward proactive, ...

Dr. Mark Pennesi looks on as staff at school's Casey Eye Institute perform the first-ever in vivo CRISPR gene edit procedure for the BRILLIANCE clinical trial in Portland. Kristyna Wentz-Graff/OHSU ...